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Creation of de novo cryptic splicing for ALS/FTD precision medicine


Authors: Oscar G Wilkins, Max Z.Y.J. Chien, Josette J. Wlaschin, Maria Pisliakova, David Thompson, Holly Digby, Rebecca L Simkin, Juan Antinao Diaz, Puja R Mehta, Matthew J. Keuss, Matteo Zanovello, Anna-Leigh Brown, Peter Harley, Annalucia Darbey, Rajvinder Karda, Elizabeth M.C. Fisher, Tom J. Cunningham, Claire E. Le Pichon, Jernej Ule, Pietro Fratta

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