A single amino acid variant in the variable region I of AAV capsid confers liver detargeting


Authors: Ruxiao Xing, Mengyao Xu, Darcy Reil, April Destefano, Mengtian Cui, Nan Liu, Jialing Liang, Guangchao Xu, Li Luo, Meiyu Xu, Fang Zhang, Phillip WL Tai, Alisha M Gruntman, Terence R Flotte, Guangping Gao, Dan Wang